• ġ, ߱  ַ
  • 20240329_ũ__
  • 20240125_ũ_
  • 20240123_ũ_繫ǥ
  • 20240117_ũ_ǿƮ
  • 20240112_ũ_ֽİġ
  • 20240108_ũ_ι
  • 20240103_ũ_ȸ繫ǥ
  • 20231229_ũ_ġڴ¿Ǵ
  • 20231222_ũ_λ

home ֽ м

[˷5] , ƽþ CRISPR ڰ õƯ㡤

| ˷5 յ 5 Ʈ ˱ Ұϴ ڳԴϴ.
1. 7 Ȯ ϴ ص

10 Ưʸ ޾ ڳؽ ڽ Ѵ. 11 25~26 俹 ߰ 2~3 Ϲ û ̴. ǥְ ѱ̴.

俹 324 ߰ 29.54 1 ߴ. Ȯ 𰡴 7̴. 10~12 ϴ 30% ص ġ. ְ ѱ ڹ Ϸκ 3 ֿ ȯû(Dzɼ) οŰ ߴ. ȯû Ⱓ ڰ 90% ǻ翡 ָ ִ Ǹ.

ڽ 򰡱  򰡸 ޾ A ̻ Ͽ ( Ưʻ)μ 11 4 忹ɻ ޾Ҵ. 迡 ڽ ̹ °. ռ 3 û ɻ縦 ߴ. ù Ư û 6⸸̴.



޵Ǵ ݾ 680̴. 2Ⱓ ޼(ڱ ÷ Ư ϡ , 162), ߺ(392), üڱ(72) ̴. ڱݼҿ ڱ ȸϴ ݾ üῡ ڱ ⿡ ȹ̴.

2. , CRISPR õ Ư㡤 ƽþ ÷

CRISPR-Cas9 õ Ư㸦 ÷ ̴. 1999 ȭк â߰ ZFN ڰ(1), TALEN ڰ(2) ߿ ̾ 2012 CRISPR/Cas9 ڰ(3) ߿ ϸ鼭 ߴ.

ٽɱ (CRISPR/Cas9) ÷ ִ ǥ DNA ãư ޶ٴ ̵ RNA(ٻ) Cas9 ܹ DNA ڸ ȿ Cas9 ¦ ̷ ü ڰ ÷ ̴.

ư ÷ ̼ Ѿ ڱ о ġ Ĺ о ϰ ִ. ġ ߴܰ迡 ǰȭ ̼ ƿ ü ޻ ϸ鼭 ܰ Ͻ ް, ǰ Ŀ Ǹž κ οƼ ϰ ȴ.

1뿡 3뿡 ̸ ȭ ܰ躰 ڰ ȸ. CRISPR/Cas9 ڰ õƯ㸦 ڱ ġ, ڱ /Ĺ ε, ڱ ġ ӻ 1 ̻󿡼 ġ κ Lead candidate ̰ų Pre-clinical ܰ迡 ִ.

ȸ ܰ ռ CAR-T ġ ȣ CARTherics 2022 Ͽ ̱ ӻ 1 ȹ̴. In vivo Programs --(CMT) ġ 2021 IND-enabling ܰ Ͽ 2022 ȿ Ȯ ̴.



(ڷ : IR BOOK)

3. ֿ 9 õƯ ϡƯȭ ñ

CRISPR ڰ õƯ㸦 ϰ ִ ƽþ ֿ 9 (ѱ/̱//ȣ/߱/Ϻ/̰/ε/ȫ) õƯ㰡 ϵǾ ִ. ڼ (Ư ǥ) 235 ϰ 48 Ư, 2 ǿž, 50 ǥ ϵǾ, 135 Ư̴.

̷ ڱ ÷ Ư㸦 Ưȭ (̼ ) ַϰ ִ. Ưȭ ڱ CRISPR ڰ õ/ Ǹ ̾ ڱ Ȯ Բ Ȯ , Ư ұ Ȯ, Ư ο  ִ.

CVC ׷, Broad Institute ˽ɻ(Interference) ϰ ִ. CRISPR ڰ õƯ ټ ڱ ޾ ˽ɻ Senior Party ġ ˷ CVC's ε Junior party 忡 ռ ߸ ߴٴ ؾϴ δ ִ.

ȸ ǰ ִ ̱ Ư ˽ɻ簡 2023 Ϸ Ǹ ˽ɻ ̱ ټ ϵ ̶ ȴٰ ߴ. ⿡ ̱ ˽ɻ ׷ ü CRISPR Ư Ǹ ̿ ߰ ű԰ ü ȴٰ ٿ.


(ڷ : IR BOOK)

4. 2023 &

Ưʸ ޾ ڽ 忡 Ѵ. ڱ ÷ 򰡸 ǷϿ 9 SCI ǿȭ(FACT)κ A ޾Ҵ.

ȸ 2013 7 ۷ι KeyGene, 2014 12 ۷ι þ Thermo Fisher Scientific, 2017 8 ۷ι ڱ Monsanto ü ࿡ ߻ߴ. ٸ ߰ Ư , η Ȯ ΰǺ ս ߴ.

ڴ " 17 ü Annual Fee, Milestone Payment Ͽ ߻ "̶ " ̱ ˽ɻ(Interference) ȸ CRISPR ڰ õƯ ߸ ׷(CVC ׷, Broad Institute) Ͽ License ̲ ϰ ִ" ߴ.

⿡ 2022ʹ HO ι Ǹŷ ߻ ̶ ߴ. ȸ 2022 21, 2023 871, 2024 1402 2023 þ ̴. Ҿ 2022 ڰ ӵǴ 2023 ڷ Ƽ δ.


(ڷ : ڼ)

5. ִ ؽ 3 ȣ 14%

ִִ ڽ ؽ̴. ؽ ֽ 1118347( 14.24%) Ϸκ 3 ѱŹ ǹŹȴ. 迵ȣ ǥ̻ 4 Ư ֽ 112332( 1.43%) Ϸκ 1Ⱓ Ű ѵȴ.

ؽ 9 濵 2 ִ ֿ ǰ üϿ 3 ȸ ǰ ϱ ִ. ֽ 68144( 8.66%) Ϸκ 3Ⱓ ڹ ǹϱ ߴ.

ڱ ߽ ȸ оߺ ȭϱ 2020 6 Ѱϴ 迵ȣ ǥ̻縦 ϸ ̺ȭ ǥ̻ ǥü ȸ縦  ̴.

迵ȣ ǥ̻(CTO) â Ͽμ ִ. 20Ⱓ ž ̸Ӻ ġ Ű溴 ġ ټ ؿ ׾. 2002~2019 ޵еƼ ǥ̻ ߰ R&D Ѱ ð ִ.

濵 Ѱϴ ̺ȭ ǥ̻(CEO) ѱſ, ũ, ޵ 2018 3 շߴ. 10, ̿ 迡 21 ̿ ؿ 繫, ũ, 濵, 濵 ݿ ɷ ϰ ִ.





ƮƮ ũα (0) ֱֱ(0)
:
|

 Ѹ ( 0)

ϴ. ù° ּ.

* HTML ± Ͻ ϴ.

Է

Powered by Stockwatch


03 / 29 14 : 42

199800

67,700 500 , 0.73 %

ֽMRI м

ڸŷµ
̼ ononononon

10

/ 25

 offoffoffoffoff
繫 ononononoff
 强 onoffoffoffoff
 â offoffoffoffoff
* ֽMRI 췮 : ּ 15 ̻
* 3 ̸ м Ⱓ   ª Ϻ ٸ ֽϴ.
20240125_ũ_20240112_ũ_ֽİġ

츮-